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Number of items: 95.

A

Argyros, O and Wong, SP and Niceta, M and Waddington, SN and Howe, SJ and Coutelle, C and Miller, AD and Harbottle, RP (2008) Persistent episomal transgene expression in liver following delivery of a scaffold/matrix attachment region containing non-viral vector. GENE THER , 15 (24) 1593 - 1605. 10.1038/gt.2008.113.

Argyros, O and Wong, SP and Niceta, M and Waddington, SN and Howe, SJ and Coutelle, C and Miller, AD and Harbottle, RP (2008) Persistent episomal transgene expression in liver following delivery of a scaffold/matrix attachment region containing non-viral vector. Gene Ther , 15 (24) 1593 - 1605. 10.1038/gt.2008.113.

B

Bainbridge, JWB and Smith, AJ and Barker, SS and Robbie, S and Henderson, R and Balaggan, K and Viswanathan, A and Holder, GE and Stockman, A and Tyler, N and Petersen-Jones, S and Bhattacharya, SS and Thrasher, AJ and Fitzke, FW and Carter, BJ and Rubin, GS and Moore, AT and Ali, RR (2008) Effect of gene therapy on visual function in Leber's congenital amaurosis. NEW ENGL J MED , 358 (21) 2231 - 2239. 10.1056/NEJMoa0802268.

Baird, SK and Aerts, JL and Eddaoudi, A and Lockley, M and Lemoine, NR and McNeish, IA (2008) Oncolytic adenoviral mutants induce a novel mode of programmed cell death in ovarian cancer. ONCOGENE , 27 (22) 3081 - 3090. 10.1038/sj.onc.1210977.

Baird, SK and Ingemarsdotter, CK and Eddaoudi, A and Lockley, M and Lemoine, NR and McNeish, IA (2008) Oncolytic adenoviral mutants define a novel mode of programmed cell death in ovarian cancer. In: HUMAN GENE THERAPY. (pp. 399 - 399). MARY ANN LIEBERT INC

Bartholomae, CC and Yanez-Munoz, RJ and Balaggan, KS and Howe, SJ and MacNeil, A and Ali, RR and Thrasher, AJ and von Kalle, C and Schmidt, M (2008) Nearly random integration site distribution in postmitotic rodent tissues transduced with lentiviral SIN-vectors. Blood Cells, Molecules, and Diseases , 40 (2) 6 - ?.

Bartholomae, CC and Yanez-Munoz, RJ and Balaggan, KS and Howe, SJ and MacNeil, A and Ali, RR and Thrasher, AJ and von Kalle, C and Schmidt, M (2008) Nearly random integration site distribution in postmitotic rodent tissues transduced with lentiviral SIN-vectors. In: BLOOD CELLS MOLECULES AND DISEASES. (pp. 253 - 253). ACADEMIC PRESS INC ELSEVIER SCIENCE

Bennour, E and Ferrand, C and Remy-Martin, JP and Certoux, JM and Gorke, S and Qasim, W and Gaspar, HB and Baumert, T and Duperrier, A and Deschamps, M and Fehse, B and Tiberghien, P and Robinet, E (2008) Abnormal expression of only the CD34 part of a transgenic CD34/herpes simplex virus-thymidine kinase fusion protein is associated with ganciclovir resistance. HUM GENE THER , 19 (7) 699 - 709. 10.1089/hum.2007.060.

Blundell, MP and Bouma, G and Calle, Y and Jones, GE and Kinnon, C and Thrasher, AJ (2008) Improvement of migratory defects in a murine model of Wiskott-Aldrich syndrome gene therapy. MOL THER , 16 (5) 836 - 844. 10.1038/mt.2008.43.

Blundell, MP and Bouma, G and Calle, Y and Jones, GE and Kinnon, C and Thrasher, AJ (2008) Restoration of migratory defects in a murine model of WiskottAldrich syndrome gene therapy. HUMAN GENE THERAPY , 19 (4) 400 - 400.

Bolda, F and Bosi, A and Baffelli, R and Qasim, W and Gaspar, B and Porta, G and Porta, F and Lanfranchi, A (2008) Role of amniotic fluid mesenchymal stem cells in gene and cell therapy. In: BONE MARROW TRANSPLANTATION. (pp. S324 - S324). NATURE PUBLISHING GROUP

Bolda, F and Bosi, A and Lorenzi, L and Porta, G and Qasim, W and Gaspar, B and Porta, F and Lanfranchi, A (2008) Role of amniotic fluid mesenchymal stem cells in gene and cell therapy. In: CLINICAL AND EXPERIMENTAL IMMUNOLOGY. (pp. 75 - 75). WILEY-BLACKWELL PUBLISHING, INC

Bonanomi, S and Connor, P and Webb, D and Ancliff, P and Amrolia, P and Rao, K and McCloskey, D and Hemmatpour, S and Goulden, N and Veys, P (2008) Successful outcome of allo-SCT in high-risk pediatric AML using chemotherapy-only conditioning and post transplant immunotherapy. Bone Marrow Transplant. , 42 (9) 635 - ?.

Bonanomi, S and Connor, P and Webb, D and Ancliff, P and Amrolia, P and Rao, K and McCloskey, D and Hemmatpour, S and Goulden, N and Veys, P (2008) Successful outcome of allo-SCT in high-risk pediatric AML using chemotherapy-only conditioning and post transplant immunotherapy. Bone Marrow Transplant , 42 (4) 253 - 257. 10.1038/bmt.2008.160.

Bosi, A and Bolda, F and Baffelli, R and Porta, G and Qasim, W and Gaspar, B and Porta, F and Lanfranchi, A (2008) ROLE OF AMNIOTIC FLUID MESENCHYMAL STEM CELLS IN CELL-BASED AND GENE THERAPY. In: HAEMATOLOGICA-THE HEMATOLOGY JOURNAL. (pp. S123 - S123). FERRATA STORTI FOUNDATION
An open access publication

Bouma, G and Mendoza-Naranjo, A and Burns, S and Thrasher, AJ (2008) Defective T-cell education by dendritic cells contributes to impaired antigen specific immunity in Wiskott-Aldrich syndrome. In: CLINICAL AND EXPERIMENTAL IMMUNOLOGY. (pp. 157 - 158). WILEY-BLACKWELL PUBLISHING, INC

Bowna, G and Doffinger, R and Patel, S and Peskett, E and Sinclair, J and Kumararatne, D and Davies, EG and Thrasher, AJ and Burns, S (2008) Neutrophil dysfunction 2 in IRAK-(4) deficiency. In: CLINICAL AND EXPERIMENTAL IMMUNOLOGY. (pp. 209 - 209). WILEY-BLACKWELL PUBLISHING, INC

Buckland, KF and Hussell, T and Lloyd, CN (2008) Development of a model of viral-induced exacerbation of allergic airways disease. In: IMMUNOLOGY. (pp. 105 - 105). WILEY-BLACKWELL PUBLISHING, INC

Buckland, KF and O'Connor, E and Murray, LA and Hogaboam, CM (2008) Toll like receptor-2 modulates both innate and adaptive immune responses during chronic fungal asthma in mice. INFLAMM RES , 57 (8) 379 - 387. 10.1007/s00011-008-8004-y.

Buckley, SM and Howe, SJ and Wong, SP and Buning, H and McIntosh, J and Baker, A and Nathwani, AC and Thrasher, A and Coutelle, C and McKay, TR and Waddington, S (2008) Luciferin detection after intra-nasal vector delivery is improved by intra-nasal rather than intra-peritoneal luciferin administration. Hum Gene Ther 10.1089/hgt.2008.023.

Buckley, SMK and Howe, SJ and Rahim, AA and Buning, H and McIntosh, J and Wong, SP and Baker, AH and Nathwani, A and Thrasher, AJ and Coutelle, C and Mckay, TR and Waddington, SN (2008) Luciferin Detection After Intranasal Vector Delivery Is Improved by Intranasal Rather Than Intraperitoneal Luciferin Administration. HUM GENE THER , 19 (10) 1050 - 1056. 10.1089/hum.2008.023.

Buckley, SMK and Howe, SJ and Sheard, V and Ward, NJ and Coutelle, C and Thrasher, AJ and Waddington, SN and Mckay, TR (2008) Lentiviral transduction of the murine lung provides efficient pseudotype and developmental stage-dependent cell-specific transgene expression. GENE THER , 15 (16) 1167 - 1175. 10.1038/gt.2008.74.

Burns, S and Hardy, S and Bouma, G and Klein, N and Thrasher, AJ (2008) Dendritic cells require CD18 for normal podosome formation. In: CLINICAL AND EXPERIMENTAL IMMUNOLOGY. (pp. 16 - 16). WILEY-BLACKWELL PUBLISHING, INC

C

Calle, Y and Anton, IM and Thrasher, AJ and Jones, GE (2008) WASP and WIP regulate podosomes in migrating leukocytes. JOURNAL OF MICROSCOPY-OXFORD , 231 (3) 494 - 505.

Cohen, JM and Cuckow, P and Davies, EG (2008) Bladder wall telangiectasis causing life-threatening haematuria in ataxia-telangiectasia: a new observation. Acta Paediatr. , 97 (5) 667 - 669.

Connor, P and Khair, K and Liesner, R and Amrolia, P and Veys, P and Ancliff, P and Mathias, M (2008) Stem cell transplantation for children with Glanzmann thrombasthenia. Br J Haematol , 140 (5) 568 - 571. 10.1111/j.1365-2141.2007.06890.x.

Connor, P and Veys, P and Amrolia, P and Haworth, S and Ashworth, M and Moledina, S (2008) Pulmonary hypertension in children with Evans syndrome. Pediatr Hematol Oncol , 25 (2) 93 - 98. 10.1080/08880010801888253.

Cooper, N and Rao, K and Goulden, N and Webb, D and Amrolia, P and Veys, P (2008) The use of reduced-intensity stem cell transplantation in haemophagocytic lymphohistiocytosis and Langerhans cell histiocytosis. Bone Marrow Transplant , 42 Suppl 2 S47 - S50. 10.1038/bmt.2008.283.

D

Deichman, A and Schmidt, M and Abina, SHB and Cavazzana-Calvo, M and Schwarzwaelder, K and Howe, SJ and Thrasher, AJ and Glimm, H and Ott, MG and Hoelzer, D and Grez, M and Seger, R and Aiuti, A and von Kalle, CN (2008) Comparative integration site profile analysis in 5 clinical retroviral gene therapy studies. Blood Cells, Molecules, and Diseases , 40 (2) 23 - ?.

Deichman, A and Schmidt, M and Abina, SHB and Cavazzana-Calvo, M and Schwarzwaelder, K and Howe, SJ and Thrasher, AJ and Glimm, H and Ott, MG and Hoelzer, D and Grez, M and Seger, R and Aiuti, A and von Kalle, CN (2008) Comparative integration site profile analysis in 5 clinical retroviral gene therapy studies. In: BLOOD CELLS MOLECULES AND DISEASES. (pp. 262 - 262). ACADEMIC PRESS INC ELSEVIER SCIENCE

G

Gabriel, R and Paruzynski, A and Eckenberg, R and Bartholomae, CC and Nowrouzi, A and Wang, W and Schwarzwaelder, K and Arens, A and Kirsten, R and Deichmann, A and Ball, C and Howe, SJ and Recchia, A and Cattoglio, C and Balaggan, KS and Yanez-Munoz, RJ and Ali, RR and Mavilio, F and Gaspar, B and Thrasher, A and Glimm, H and von Kalle, C and Saurin, W and Schmidt, M (2008) Comprehensive and Unbiased Integration Site Analysis in Clinical Gene Therapy. In: BLOOD. (pp. 819 - 819). AMER SOC HEMATOLOGY

Gabriel, R and Paruzynski, A and Eckenberg, R and Bartholomae, CC and Nowrouzi, A and Wang, W and Schwarzwaelder, K and Arens, A and Kirsten, R and Deichmann, A and Ball, CR and Howe, SJ and Recchia, A and Claudia, C and Balaggan, KS and Yanez-Munoz, RJ and Ali, RR and Mavilio, F and Gaspar, HB and Thrasher, AJ and Glimm, H and von Kalle, C and Saurin, W and Schmidt, M (2008) Assessing the genome accessibility of viral integration sites. HUMAN GENE THERAPY , 19 (10) 1085 - 1085.

Galy, A and Roncarolo, M-G and Thrasher, AJ (2008) Development of lentiviral gene therapy for Wiskott Aldrich syndrome. Expert Opinion on Biological Therapy , 8 (2) 181 - 190.

Gaspar, HB and Bjorkegren, E and Parsley, K and Gilmour, K and Fairbanks, L and Zhang, F and Giannakopoulos, A and King, D and Adams, S and Bayford, JX and Henderson, L and Davies, G and Veys, P and Thrasher, AJ (2008) Reconstitution of immune function in adenosine deaminase deficient severe combined immunodeficiency following hematopoietic stem cell gene therapy. In: BLOOD CELLS MOLECULES AND DISEASES. (pp. 266 - 267). ACADEMIC PRESS INC ELSEVIER SCIENCE

Greystoke, B and Bonanomi, S and Carr, TF and Gharib, M and Khalid, T and Coussons, M and Jagani, M and Naik, P and Rao, K and Goulden, N and Amrolia, P and Wynn, RF and Veys, PA (2008) Treosulfan-containing regimens achieve high rates of engraftment associated with low transplant morbidity and mortality in children with non-malignant disease and significant co-morbidities. Br J Haematol , 142 (2) 257 - 262. 10.1111/j.1365-2141.2008.07064.x.

H

Herzog, RW (2008) Immunology of Gene Therapy. Wiley-Blackwell

Himoudi, N and Nabarro, S and Buddle, J and Eddaoudi, A and Thrasher, AJ and Anderson, J (2008) Bone marrow-derived IFN-producing killer dendritic cells account for the tumoricidal activity of unpulsed dendritic cells. J Immunol , 181 (9) 6654 - 6663.

Himoudi, N and Nabarro, S and Buddle, J and Eddaoudi, A and Thrasher, AJ and Anderson, J (2008) Bone Marrow-Derived IFN-Producing Killer Dendritic Cells Account for the Tumoricidal Activity of Unpulsed Dendritic Cells. J IMMUNOL , 181 (9) 6654 - 6663.

Himoudi, N and Nabarro, S and Buddle, J and Eddaoudi, A and Thrasher, AJ and Anderson, J (2008) Bone marrow-derived IFN-producing killer dendritic cells account for the tumoricidal activity of unpulsed dendritic cells. Journal of Immunology , 181 (9) 6654 - 6663.

Himoudi, N and Yan, MY and Papanastasiou, A and Anderson, J (2008) MYCN as a target for cancer immunotherapy. CANCER IMMUNOL IMMUN , 57 (5) 693 - 700. 10.1007/s00262-007-0409-x.

Hiwarkar, P and Arkenau, HT and Treleaven, J and Morgan, G and Potter, M and Ethell, M (2008) The feasibility of using topotecan, vinorelbine, thiotepa and gemcitabine (TVTG) in adult patients with relapsed/refractory acute lymphoblastic leukaemia/lymphoma. LEUKEMIA , 22 (8) 1627 - 1629. 10.1038/leu.2008.31.

Hiwarkar, P and Kulkarni, S and Dungarwalla, M and Saso, R and Shaw, B and Evans, S and Treleaven, J and Morgan, G and Ethell, M and Potter, M (2008) Mycophenolic acid trough level monitoring in graft-versus-host disease treated with Mycophenolate mofetil: correlation with albumin levels and clinical response. In: BONE MARROW TRANSPLANTATION. (pp. S224 - S224). NATURE PUBLISHING GROUP

Howe, SJ and Mansour, M and Brugman, M and Pike-Overzet, K and Hubank, M and Jina, N and de Ridder, D and Staal, F and Baum, C and Kinnon, C and Gaspar, HB and Thrasher, AJ (2008) Molecular analysis of a severe adverse event in the UKSCID-X1 gene therapy clinical trial. In: HUMAN GENE THERAPY. (pp. 421 - 421). MARY ANN LIEBERT INC

Howe, SJ and Mansour, M and Brugman, M and Pike-Overzet, K and Hubank, M and Jina, N and de Ridder, D and Staal, F and Baum, C and Kinnon, C and Gaspar, HB and Thrasher, AJ (2008) Molecular analysis of a severe adverse event in the UKSCID-X1 gene therapy clinical trial. Human Gene Therapy , 19 (4) 82 - ?.

Howe, SJ and Mansour, MR and Schwarzwaelder, K and Bartholomae, C and Hubank, M and Kempski, H and Brugman, MH and Pike-Overzet, K and Chatters, SJ and de Ridder, D and Gilmour, KC and Adams, S and Thornhill, SI and Parsley, KL and Staal, FJT and Gale, RE and Linch, DC and Bayford, J and Brown, L and Quaye, M and Kinnon, C and Ancliff, P and Webb, DK and Schmidt, M and von Kalle, C and Gaspar, HB and Thrasher, AJ (2008) Insertional mutagenesis combined with acquired somatic mutations causes leukemogenesis following gene therapy of SCID-X1 patients. J CLIN INVEST , 118 (9) 3143 - 3150. 10.1172/JCI35798.
An open access publication

Howe, SJ and Mansour, MR and Schwarzwaelder, K and Bartholomae, C and Hubank, M and Kempski, H and Brugman, MH and Pike-Overzet, K and Chatters, SJ and De Ridder, D and Gilmour, KC and Adams, S and Thornhill, SI and Parsley, KL and Staal, FJT and Gale, RE and Linch, DC and Bayford, J and Brown, L and Quaye, M and Kinnon, C and Ancliff, P and Webb, DK and Schmidt, M and Von Kalle, C and Gaspar, HB and Thrasher, AJ (2008) Insertional mutagenesis combined with acquired somatic mutations causes leukemogenesis following gene therapy of SCID-X1 patients. Journal of Clinical Investigation , 118 (9) 3143 - 3150.

Hunter, P and Ana, N and Nistala, K and Eddaoudi, A and Hubank, M and Wedderbum, LR (2008) Molecular tools with which to predict extension to severe disease in oligoarticular juvenile idiopathic arthritis (JIA). In: ARTHRITIS AND RHEUMATISM. (pp. S409 - S410). WILEY-LISS

Hunter, P and Eddaoudi, A and Jina, N and Shah, S and Pallas, J and Hubank, M and Wedderburn, LR (2008) Size of CD8 T cell compartment in synovial fluid predicts extension in children with oligoarticular juvenile idiopathic arthritis. In: ANNALS OF THE RHEUMATIC DISEASES. (pp. A14 - A15). B M J PUBLISHING GROUP

Hunter, PJ and Eddaoudi, A and Jina, N and Shah, S and Pallas, J and Hubank, M and Wedderburn, LR (2008) Size of CD8T cell compartment in synovial fluid predicts extension in children with oligoarticular juvenile idiopathic arthritis. In: RHEUMATOLOGY. (pp. II19 - II19). OXFORD UNIV PRESS

Hurley, CA and Wong, JB and Ho, J and Writer, M and Irvine, SA and Lawrence, MJ and Hart, SL and Tabor, AB and Hailes, HC (2008) Mono- and dicationic short PEG and methylene dioxyalkylglycerols for use in synthetic gene delivery systems. ORG BIOMOL CHEM , 6 (14) 2554 - 2559. 10.1039/b719702k.

I

Irvine, SA and Meng, QH and Afzal, F and Ho, J and Wong, JB and Hailes, HC and Tabor, AB and McEwan, JR and Hart, SL (2008) Receptor-targeted nanocomplexes optimized for gene transfer to primary vascular cells and explant cultures of rabbit aorta. MOL THER , 16 (3) 508 - 515. 10.1038/sj.mt.6300381.

J

Jones, LBKR and McGrogan, P and Flood, TJ and Gennery, AR and Morton, L and Thrasher, A and Goldblatt, D and Parker, L and Cant, AJ (2008) Special Article: Chronic granulomatous disease in the United Kingdom and Ireland: a comprehensive national patient-based registry. CLINICAL AND EXPERIMENTAL IMMUNOLOGY , 152 (2) 211 - 218. 10.1111/j.1365-2249.2008.03644.x.

K

Kao, V and Waddington, S and Thrasher, A and Antoniou, M (2008) Novel lentiviral vectors for haemophilia gene therapy. In: HUMAN GENE THERAPY. (pp. 1134 - 1134).

Kao, V and Waddington, S and Thrasher, A and Antoniou, M (2008) Novel lentiviral vectors for targeting the red blood cell lineage. HUMAN GENE THERAPY , 19 (4) 415 - 415.

Karlsson, H and Samarasinghe, S and Ball, LM and Sundberg, B and Lankester, AC and Dazzi, F and Uzunel, M and Rao, K and Veys, P and Le Blanc, K and Ringdén, O and Amrolia, PJ (2008) Mesenchymal stem cells exert differential effects on alloantigen and virus-specific T-cell responses. Blood , 112 (3) 532 - 541. 10.1182/blood-2007-10-119370.

Knight, S and Bokhoven, M and Gupta, A and Ceylan, M and Zhang, F and Antoniou, M and Thrasher, A and Takeuchi, Y and Collins, M (2008) Insertional mutagenesis by retroviral and lentiviral vectors. In: HUMAN GENE THERAPY. (pp. 1190 - 1190). MARY ANN LIEBERT INC

L

Le Deist, F and Moshous, D and Howe, SJ and Nahum, A and Kavadas, F and Lavine, D and Roifman, CM and Fischer, A (2008) Combined T and B Cell Immunodeficiencies. In: Rezaei, N and Aghamohammadi, A and Notarangelo, LD, (eds.) Primary Immunodeficiency Diseases: Definition, Diagnosis, and Management. Springer

M

Meyer-Bahlburg, A and Becker-Herman, S and Humblet-Baron, S and Khim, S and Weber, M and Bouma, G and Thrasher, AJ and Batista, FD and Rawlings, DJ (2008) Wiskott-Aldrich syndrome protein deficiency in B cells results in impaired peripheral homeostasis. BLOOD , 112 (10) 4158 - 4169. 10.1182/blood-2008-02-140814.

Montiel-Equihua, CA and Martin-Duque, P and de la Vieja, A and Quintanilla, M and Burnet, J and Vassaux, G and Lemoine, NR (2008) Targeting sodium/iodide symporter gene expression for estrogen-regulated imaging and therapy in breast cancer. CANCER GENE THER , 15 (7) 465 - 473. 10.1038/cgt.2008.6.

O

Ozsahin, H and Cavazzana-Calvo, M and Notarangelo, LD and Schulz, A and Thrasher, AJ and Mazzolari, E and Slatter, MA and Le Deist, F and Blanche, S and Veys, P and Fasth, A and Bredius, R and Sedlacek, P and Wulffraat, N and Ortega, J and Heilmann, C and O'Meara, A and Wachowiak, J and Kalwak, K and Matthes-Martin, S and Gungor, T and Ikinciogullari, A and Landais, P and Cant, AJ and Friedrich, W and Fischer, A (2008) Long-term outcome following hematopoietic stem-cell transplantation in Wiskott-Aldrich syndrome: collaborative study of the European Society for Immunodeficiencies and European Group for Blood and Marrow Transplantation. BLOOD , 111 (1) 439 - 445. 10.1182/blood-2007-03-076679.

P

Pilkington-Miksa, MA and Sarkar, S and Writer, MJ and Barker, SE and Shamlou, PA and Hart, SL and Hailes, HC and Tabor, AB (2008) Synthesis of bifunctional integrin-binding peptides containing PEG spacers of defined length for non-viral gene delivery. European Journal of Organic Chemistry (17) 2900 - 2914.

Pilkington-Miksa, MA and Sarkar, S and Writer, MJ and Barker, SE and Shamlou, PA and Hart, SL and Hailes, HC and Tabor, AB (2008) Synthesis of bifunctional integrin-binding peptides containing PEG spacers of defined length for non-viral gene delivery. EUR J ORG CHEM (17) 2900 - 2914. 10.1002/ejoc.200701188.

R

Rahim, AA and Waddington, SN and Wong, AMS and Ward, NJ and Elston, KE and Buckley, SMK and Philpott, NJ and Cooper, JD and Anderson, PN and Thrasher, AJ and Raivich, G (2008) Efficient gene delivery to the adult and fetal central nervous system using pseudotyped non-integrating lentiviral vectors. In: HUMAN GENE THERAPY. (pp. 398 - 398). MARY ANN LIEBERT INC

Ricciardelli, I and Lindley, KJ and Londei, M and Quaratino, S (2008) Anti tumour necrosis-alpha therapy increases the number of FOXP3(+) regulatory T cells in children affected by Crohn's disease. IMMUNOLOGY , 125 (2) 178 - 183. 10.1111/j.1365-2567.2008.02839.x.

S

Salzer, US and Bacchelli, C and Buckridge, S and Pan-Hammar-Strom, Q and Jennings, S and Lougaris, V and Bergbreiter, A and Hagena, T and Birmelin, J and Plebani, A and Webster, ADB and Peter, HH and Suez, D and Chapel, H and Maclean-Tooke, A and Spickett, GP and Anover-Sombke, S and Ochs, HD and Urschel, S and Belohradsky, BH and Ugrinovic, S and Kumararatne, DS and Lawrence, TC and Holm, AM and Franco, JL and Schulze, I and Schneider, P and Gertz, ME and Schaffer, AA and Hammarstrom, L and Thrasher, AJ (2008) Relevance of biallelic vs monoallelic TNFRSF13B mutations in distinguishing disease-causing from risk-increasing TNFRSF13B variants in antibody deficiency syndromes. CLINICAL AND EXPERIMENTAL IMMUNOLOGY , 154 207 - 208.

Santilli, G and Blundell, M and Haria, S and Kinnon, C and Antoniou, M and Grez, M and Thrasher, A (2008) Evaluation of self-inactivating lentiviral vectors containing myeloid specific promoters in combination with the ubiquitously acting chromatin opening element (UCOE) for gene therapy of X-CGD. In: HUMAN GENE THERAPY. (pp. 417 - 417). MARY ANN LIEBERT INC

Santilli, G and Thornhill, SI and Christine, K and Thrasher, AJ (2008) Gene therapy of inherited immunodeficiencies. EXPERT OPIN BIOL TH , 8 (4) 397 - 407. 10.1517/14712598.8.4.397.

Satwani, P and Cooper, N and Rao, K and Veys, P and Amrolia, P (2008) Reduced intensity conditioning and allogeneic stem cell transplantation in childhood malignant and nonmalignant diseases. Bone Marrow Transplant , 41 (2) 173 - 182. 10.1038/sj.bmt.1705923.

Schwab, R and Bussolari, R and Corvetta, D and Chayka, O and Santilli, G and Kwok, JMM and Amorotti, GF and Tonini, GP and Iacoviello, L and Bertorelle, R and Menin, C and Hubank, M and Calabretta, B and Sala, A (2008) Isolation and functional assessment of common, polymorphic variants of the B-MYB proto-oncogene associated with a reduced cancer risk. ONCOGENE , 27 (20) 2929 - 2933. 10.1038/sj.onc.1210947.

Schwarzwaelder, K and Schmidt, M and Deichmann, A and Howe, S and Ott, MG and Stein, S and Siler, U and Hacein-Bey-Abina, S and Glimm, H and Hoelzer, D and Cavazzana-Calvo, M and Thrasher, A and Seger, R and Grez, M and von Kalle, C (2008) The gene corrected clonal inventory in clinical gene therapy trials. Blood Cells, Molecules, and Diseases , 40 (2) 66 - ?.

Schwarzwaelder, K and Schmidt, M and Deichmann, A and Howe, S and Ott, MG and Stein, S and Siler, U and Hacein-Bey-Abina, S and Glimm, H and Hoelzer, D and Cavazzana-Calvo, M and Thrasher, A and Seger, R and Grez, M and von Kalle, C (2008) The gene corrected clonal inventory in clinical gene therapy trials. In: BLOOD CELLS MOLECULES AND DISEASES. (pp. 284 - 284).

Staples, ER and McDermott, EM and Reiman, A and Byrd, PJ and Ritchie, S and Taylor, AM and Davies, EG (2008) Immunodeficiency in ataxia telangiectasia is correlated strongly with the presence of two null mutations in the ataxia telangiectasia mutated gene. Clin.Exp.Immunol. , 153 (2) 214 - 220.

Stein, S and Ott, MG and Schultze-Strasser, S and Jauch, A and Burwinkel, B and Schmidt, M and Martin, H and Koehl, U and Preiss, C and Rudolf, E and Kunkel, H and Schwarzwaelder, K and Hofmann, WK and Kuehlcke, K and Schlegelberger, B and Thrasher, AJ and Seger, R and von Kalle, C and Hoelzer, D and Grez, M (2008) Gene therapy for chronic granulomatous disease: Current status of the German clinical study. In: HUMAN GENE THERAPY. (pp. 1097 - 1097). MARY ANN LIEBERT INC

T

Tagalakis, AD and McAnulty, RJ and Devaney, J and Bottoms, SE and Wong, JB and Elbs, M and Writer, MJ and Hailes, HC and Tabor, AB and O'Callaghan, C and Jaffe, A and Hart, SL (2008) A receptor-targeted nanocomplex vector system optimized for respiratory gene transfer. MOL THER , 16 (5) 907 - 915. 10.1038/mt.2008.38.

Talbot, GE and Qasim, W and Thrasher, AJ and Harper, JI and Di, WL (2008) Reproducible and stable transgene expression towards ex vivo lentiviral gene therapy for Netherton syndrome. In: BRITISH JOURNAL OF DERMATOLOGY. (pp. 889 - 890). BLACKWELL PUBLISHING

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Thornhill, SI and Schambach, A and Howe, SJ and Ulaganathan, M and Grassman, E and Williams, D and Schiedlmeier, B and Sebire, NJ and Gaspar, HB and Kinnon, C and Baum, C and Thrasher, AJ (2008) Self-inactivating gammaretroviral vectors for gene therapy of x-linked severe combined immunodeficiency. Molecular Therapy , 16 (3) 590 - 598.

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Thornhill, SI and Thrasher, AJ (2008) Gene therapy for severe combined immunodeficiency: Success and risk. Biochemist , 30 (3) 26 - 29.

Thrasher, AJ (2008) Gene therapy for primary immunodeficiencies. IMMUNOL ALLERGY CLIN , 28 (2) 457 - +. 10.1016/j.iac.2008.02.001.

Titman, P and Pink, E and Skucek, E and O'Hanlon, K and Cole, TJ and Gaspar, J and Xu-Bayford, J and Jones, A and Thrasher, AJ and Davies, EG and Veys, PA and Gaspar, HB (2008) Cognitive and behavioral abnormalities in children after hematopoietic stem cell transplantation for severe congenital immunodeficiencies. BLOOD , 112 (9) 3907 - 3913. 10.1182/blood-2008-04-151332.

Titman, P and Pink, E and Skucek, E and O'Hanlon, K and Cole, TJ and Gaspar, J and Xu-Bayford, J and Jones, A and Thrasher, AJ and Davies, EG and Veys, PA and Gaspar, HB (2008) Cognitive and behavioral abnormalities in children after hematopoietic stem cell transplantation for severe congenital immunodeficiencies. Blood , 112 (9) 3907 - 3913.

Titman, P and Pink, E and Skucek, E and O'Hanlon, K and Cole, TJ and Gaspar, J and Xu-Bayford, J and Jones, A and Thrasher, AJ and Davies, EG and Veys, PA and Gaspar, HB (2008) Cognitive and behavioral abnormalities in children after hematopoietic stem cell transplantation for severe congenital immunodeficiencies. Blood , 112 (9) 3907 - 3913. 10.1182/blood-2008-04-151332.

Toscano, MG and Frecha, C and Benabdellah, K and Cobo, M and Blundell, M and Thrasher, AJ and Garcia-Olivares, E and Molina, IJ and Martin, F (2008) Hematopoietic-specific lentiviral vectors circumvent cellular toxicity due to ectopic expression of Wiskott-Aldrich syndrome protein. HUM GENE THER , 19 (2) 179 - 197. 10.1089/hum.2007.098.

Touvrey, C and Couedel, C and Soulas, P and Couderc, R and Jasin, M and de Villartay, JP and Marche, PN and Jouvin-Marche, E and Candeias, SM (2008) Distinct effects of DNA-PKcs and Artemis inactivation on signal joint formation in vivo. MOL IMMUNOL , 45 (12) 3383 - 3391. 10.1016/j.molimm.2008.04.004.

W

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Worth, AJJ and Cory, GOC and Thrasher, AJ and Burns, S (2008) Molecular pathogenesis of Wiskott-Aldrich syndrome mutations: insights into the mechanisms of endritic cell migration. In: CLINICAL AND EXPERIMENTAL IMMUNOLOGY. (pp. 71 - 72). WILEY-BLACKWELL PUBLISHING, INC

Y

Yan, MY and Himoudi, N and Pule, M and Sebire, N and Poon, E and Blair, A and Williams, O and Anderson, J (2008) Development of cellular immune responses against PAX5, a novel target for cancer immunotherapy. CANCER RES , 68 (19) 8058 - 8065. 10.1158/0008-5472.CAN-08-0153.

Z

Zhan, H and Cooper, N and Gaspar, H and Qasim, W (2008) Re-programming T cells through lentiviral mediated FOXP3 expression. In: HUMAN GENE THERAPY. (pp. 1139 - 1139). MARY ANN LIEBERT INC

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Zhang, F and Antoniou, M and Thrasher, A (2008) Ubiquitous chromatin opening element (UCOE)-driven transgenes within lentiviral vectors are not subject to DNA methylation mediated silencing. In: HUMAN GENE THERAPY. (pp. 1093 - 1093). MARY ANN LIEBERT INC

This list was generated on Thu May 23 10:26:34 2013 BST.