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Number of items: 82.


Abdul-Razak, HH; Rocca, C; Howe, SJ; Estevez, FJM; Gan, CHV; Roberts, A; ... Yanez-Munoz, RJ; + view all (2010) Towards Correction of the scid Mouse by Gene Targeting. In: HUMAN GENE THERAPY. (pp. 521 - 522). MARY ANN LIEBERT INC

Al-Jamal, KT; Toma, FM; Yilmazer, A; Ali-Boucetta, H; Nunes, A; Herrero, MA; ... Kostarelo, K; + view all (2010) Enhanced cellular internalization and gene silencing with a series of cationic dendron-multiwalled carbon nanotube:siRNA complexes. FASEB J , 24 (11) 4354 - 4365. 10.1096/fj.09-141036.

Albert, MH; Bittner, TC; Nonoyama, S; Notarangelo, LD; Burns, S; Imai, K; ... Ochs, HD; + view all (2010) X-linked thrombocytopenia (XLT) due to WAS mutations: clinical characteristics, long-term outcome, and treatment options. BLOOD , 115 (16) 3231 - 3238. 10.1182/blood-2009-09-239087.

Alvares, CL; Schenk, T; Hulkki, S; Min, T; Vijayaraghavan, G; Yeung, J; ... Morgan, GJ; + view all (2010) Non-cycling cells from acute myeloid leukaemia patients harbor the FLT3-ITD (FMS-like tyrosine kinase 3-internal tandem duplication) mutation and exhibit in vitro insensitivity to TKI258, a potent FLT3-directed inhibitor. In: BRITISH JOURNAL OF HAEMATOLOGY. (pp. 17 - 18). WILEY-BLACKWELL PUBLISHING, INC


Bartolovic, K; Mongkoldhumrongkul, N; Waddington, SN; Jayasinghe, SN; Howe, SJ; (2010) The differentiation and engraftment potential of mouse hematopoietic stem cells is maintained after bio-electrospray. ANALYST , 135 (1) 157 - 164. 10.1039/b917813a.

Binny, CJ; McIntosh, JH; Tuddenham, E; Waddington, S; Buckley, S; Thrasher, A; ... Davidoff, A; + view all (2010) Assessing the Potential of Perinatal Gene Transfer Using Congenital Factor VII Deficiency as a Model System. In: BLOOD. (pp. 114 - 114). AMER SOC HEMATOLOGY

Blundell, MP; Worth, A; Bouma, G; Thrasher, AJ; (2010) The Wiskott-Aldrich syndrome: The actin cytoskeleton and immune cell function. DIS MARKERS , 29 (3-4) 157 - 175. 10.3233/DMA-2010-0735.

Bordon, V; Gennery, AR; Slatter, MA; Vandecruys, E; Laureys, G; Veys, P; ... Inborn Error Working Party of the European Bone Marrow Transplantation (EBMT) group,; + view all (2010) Clinical and immunologic outcome of patients with cartilage hair hypoplasia after hematopoietic stem cell transplantation. Blood , 116 (1) 27 - 35. 10.1182/blood-2010-01-259168.

Bouma, G; Ancliff, PJ; Thrasher, AJ; Burns, SO; (2010) Recent advances in the understanding of genetic defects of neutrophil number and function. BRIT J HAEMATOL , 151 (4) 312 - 326. 10.1111/j.1365-2141.2010.08361.x.

Brewin, J.J.; (2010) Generation of calcineurin inhibitor resistant EBV-CTLs for the treatment of post transplant lymphoma. Doctoral thesis, UCL (University College London). Green open access

Burns, SO; Killock, DJ; Moulding, DA; Metelo, J; Nunes, J; Taylor, RR; ... Ivetic, A; + view all (2010) A congenital activating mutant of WASp causes altered plasma membrane topography and adhesion under flow in lymphocytes. BLOOD , 115 (26) 5355 - 5365. 10.1182/blood-2009-08-236174.


Carmo, M; Booth, C; Montiel-Equihua, CA; Schambach, A; Baum, C; Thrasher, AJ; Gaspar, HB; (2010) Development of gene therapy for haemophagocytic lymphohistiocytosis (HLH) due to perforin deficiency. In: HUMAN GENE THERAPY. (pp. 1455 - 1455). MARY ANN LIEBERT INC

Carmo, M; Booth, C; Montiel-Equihua, CA; Schambach, A; Baum, C; Thrasher, AJ; Gaspar, HB; (2010) Development of Gene Therapy for HLH Due to Perforin Deficiency. In: HUMAN GENE THERAPY. (pp. 508 - 509). MARY ANN LIEBERT INC

Chan, E; Schaller, T; Klein, N; Thrasher, A; Towers, G; Qasim, W; (2010) Lentiviral Delivery of TRIM-Cyclophilin Restriction Factors Against HIV-1. In: HUMAN GENE THERAPY. (pp. 502 - 502). MARY ANN LIEBERT INC

Chick, H; McDonald, RA; Kritz, AB; Kane, NM; Alba, R; Sessa, WC; ... Baker, AH; + view all (2010) Effect of Nogo-B Overexpression in Vascular Smooth Muscle Cell Migration and Proliferation Mediated by Integration-Deficient Lentiviral Vectors. In: HUMAN GENE THERAPY. (pp. 1203 - 1204). MARY ANN LIEBERT INC

Chick, HE; McDonald, RA; Kritz, AB; Kane, NM; Alba, R; Sessa, WC; ... Baker, AH; + view all (2010) Analysing the Effect of Nogo-B Overexpression in Vascular Smooth Muscle Cell Proliferation and Migration Induced by Non-Integrating or Integrating Lentiviral Vectors. In: HUMAN GENE THERAPY. (pp. 519 - 520). MARY ANN LIEBERT INC

Chiesa, R; Hiwarkar, P; Rao, K; Qasim, W; Gilmour, K; Goulden, N; ... Veys, P; + view all (2010) Rapid Expansion of Naive CD4+Cord Blood Lymphocytes Restores Adaptive Immunity within 2 Months After Unrelated Cord Blood Transplantation. In: BLOOD. (pp. 966 - 966). AMER SOC HEMATOLOGY

Couedel, C; Roman, C; Jones, A; Vezzoni, P; Villa, A; Cortes, P; (2010) Analysis of mutations from SCID and Omenn syndrome patients reveals the central role of the Rag2 PHD domain in regulating V(D)J recombination. J CLIN INVEST , 120 (4) 1337 - 1344. 10.1172/JCI41305.


Davies, EG; Thrasher, AJ; (2010) Update on the hyper immunoglobulin M syndromes. Br J Haematol , 149 (2) 167 - 180. 10.1111/j.1365-2141.2010.08077.x.

de Boer, J; Yeung, J; Ellu, J; Ramanujachar, R; Solarska, O; Hubank, M; ... Brady, H; + view all (2010) E2A-HLF ACTS THROUGH LMO2 AND BCL-2 TO IMMORTALIZE LYMPHOID PROGENITORS. In: HAEMATOLOGICA-THE HEMATOLOGY JOURNAL. (pp. 484 - 485). FERRATA STORTI FOUNDATION Gold open access

De Falco, E; Parsley, K; Blundell, M; Bouma, G; Gilmour, K; Lopez-Begg, D; ... Thrasher, A; + view all (2010) Development of a GMP-Grade Transduction Protocol for Treatment of the Wiskott-Aldrich Syndrome by Lentiviral Vector-Mediated Gene Therapy. In: HUMAN GENE THERAPY. (pp. 508 - 508). MARY ANN LIEBERT INC

Di, WL; Archer, F; Semenova, E; Talbot, GE; Harper, JI; Del Rio, M; ... Qasim, W; + view all (2010) Ex-vivo gene therapy restores LEKTI activity and corrects the architecture of Netherton syndrome derived skin grafts. JOURNAL OF INVESTIGATIVE DERMATOLOGY , 130 S75 - S75.


Eddaoudi, A; Townsend-Nicholson, A; Timms, JF; Schorge, S; Jayasinghe, SN; (2010) Molecular characterisation of post-bio-electrosprayed human brain astrocytoma cells. ANALYST , 135 (10) 2600 - 2612. 10.1039/c0an00213e.


Fassone, E; Duncan, AJ; Taanman, JW; Pagnamenta, AT; Sadowski, MI; Holand, T; ... Rahman, S; + view all (2010) FOXRED1, encoding an FAD-dependent oxidoreductase complex-I-specific molecular chaperone, is mutated in infantile-onset mitochondrial encephalopathy. HUM MOL GENET , 19 (24) 4837 - 4847. 10.1093/hmg/ddq414.

Ferreira, S; Kao, V; Waddington, S; Fang, Z; Ward, N; Thrasher, AJ; Antoniou, MN; (2010) Development of In Utero Lentiviral Vector Gene Therapy Approaches for Inherited Diseases. In: HUMAN GENE THERAPY. (pp. 524 - 524). MARY ANN LIEBERT INC

Field, AC; Stauss, HJ; Goulden, N; Morris, E; Qasim, W; (2010) Defining an Optimal Promoter for Lentiviral Gene Expression of T Cell Receptor Genes. In: HUMAN GENE THERAPY. (pp. 509 - 510). MARY ANN LIEBERT INC

Flutter, B; Edwards, N; Fallah-Arani, F; Henderson, S; Chai, JG; Sivakumaran, S; ... Chakraverty, R; + view all (2010) Nonhematopoietic antigen blocks memory programming of alloreactive CD8(+) T cells and drives their eventual exhaustion in mouse models of bone marrow transplantation. J CLIN INVEST , 120 (11) 3855 - 3868. 10.1172/JCI41446.

Flutter, BR; Fallah-Arani, F; Sivakumaran, S; Bennett, CL; Ghorashian, S; Freeman, G; Sykes, M; (2010) Failure to imprint donor CD8 memory and exhaustion may explain loss of GVT responses following donor leukocyte infusions. In: BONE MARROW TRANSPLANTATION. (pp. S16 - S16). NATURE PUBLISHING GROUP

Foster, K.E.; (2010) The role of neural crest cells in the development, organisation and migration of the thymus. Doctoral thesis, UCL (University College London). Green open access


Gaspar, HB; (2010) Bone Marrow Transplantation and Alternatives for Adenosine Deaminase Deficiency. IMMUNOL ALLERGY CLIN , 30 (2) 221 - +. 10.1016/j.iac.2010.01.002.

Georgiadis, A; Tschernutter, M; Bainbridge, JWB; Balaggan, KS; Mowat, F; West, EL; ... Ali, RR; + view all (2010) The Tight Junction Associated Signalling Proteins ZO-1 and ZONAB Regulate Retinal Pigment Epithelium Homeostasis in Mice. PLOS ONE , 5 (12) , Article e15730. 10.1371/journal.pone.0015730. Green and gold open access

Ghorashian, S; Wright, G; Thomas, S; Hart, D; King, J; Voisine, C; ... Stauss, H; + view all (2010) Optimising adoptive T cell therapy following allogeneic haematopoietic stem cell transplantation. In: Reisner, Y and Martelli, M, (eds.) Bone Marrow Transplantation across major genetic barriers. World Scientific Publishing Company, Incorporated

Ginn, SL; Liao, SH; Dane, AP; Zheng, M; Alexander, IE; Hu, M; ... Thrasher, AJ; + view all (2010) Lymphomagenesis in SCID-X1 mice following lentivirus-mediated phenotype correction independent of insertional mutagenesis and γc overexpression. Molecular Therapy , 18 (5) 965 - 976. 10.1038/mt.2010.50.

Gonitel, R; Acosta-Saltos, C; T, MJ; Anderson, P; Raivich, G; Thrasher, A; (2010) Non-Integrating Polycistronic Lentiviral Vectors for Use in the Central Nervous System. In: HUMAN GENE THERAPY. (pp. 511 - 512). MARY ANN LIEBERT INC

Grosse, SM; Tagalakis, AD; Mustapa, MFM; Elbs, M; Meng, QH; Mohammadi, A; ... Hart, SL; + view all (2010) Tumor-specific gene transfer with receptor-mediated nanocomplexes modified by polyethylene glycol shielding and endosomally cleavable lipid and peptide linkers. FASEB J , 24 (7) 2301 - 2313. 10.1096/fj.09-144220.


Hart, SL; (2010) Multifunctional nanocomplexes for gene transfer and gene therapy. CELL BIOL TOXICOL , 26 (1) 69 - 81. 10.1007/s10565-009-9141-y.

Hislop, AD; Palendira, U; Leese, AM; Arkwright, PD; Rohrlich, PS; Tangye, SG; ... Rickinson, AB; + view all (2010) Impaired Epstein-Barr virus-specific CD8(+) T-cell function in X-linked lymphoproliferative disease is restricted to SLAM family-positive B-cell targets. BLOOD , 116 (17) 3249 - 3257. 10.1182/blood-2009-09-238832.

Hiwarkar, P; Boyle, FO; Karnik, L; New, H; Szydlo, R; Roberts, I; de la Fuente, J; (2010) Veno Occlusive Disease After Haematopoietic Stem Cell Transplantation for beta Thalassaemia Major Is Predicted by the Severity of Hepatic Fibrosis and Ameliorated by Defibrotide. In: BLOOD. (pp. 570 - 570). AMER SOC HEMATOLOGY

Hiwarkar, P; Stasi, R; Sutherland, G; Shannon, M; (2010) Deep vein and intracardiac thrombosis during the post-partum period in Behcet's disease. INT J HEMATOL , 91 (4) 679 - 686. 10.1007/s12185-010-0538-4.

Hunter, PJ; Nistala, K; Jina, N; Eddaoudi, A; Thomson, W; Hubank, M; Wedderburn, LR; (2010) Biologic Predictors of Extension of Oligoarticular Juvenile Idiopathic Arthritis as Determined From Synovial Fluid Cellular Composition and Gene Expression. ARTHRITIS RHEUM-US , 62 (3) 896 - 907. 10.1002/art.27284. Gold open access


Joly, P; Chavda, N; Eddaoudi, A; Jayasinghe, SN; (2010) Bio-electrospraying and aerodynamically assisted bio-jetting whole human blood: Interrogating cell surface marker integrity. BIOMICROFLUIDICS , 4 (1) , Article 011101. 10.1063/1.3294083.


Kamaly, N; Kalber, T; Kenny, G; Bell, J; Jorgensen, M; Miller, A; (2010) A novel bimodal lipidic contrast agent for cellular labelling and tumour MRI. Org. Biomol. Chem. , 8 201-211 - 201-211. 10.1039/B910561A.

Kane, NM; Nowrouzi, A; Greig, JA; Houslay, MD; Milligan, G; Mountford, JC; ... Baker, AH; + view all (2010) Induction of iPS cells from Dermal Fibroblasts by High Dose HIV-Based LV Vectors in the Absence of Reprogramming Factors: Analysis of Integration Sites and Genomic Stability. In: HUMAN GENE THERAPY. (pp. 500 - 501). MARY ANN LIEBERT INC

Kane, NM; Nowrouzi, A; Mukherjee, S; Blundell, MP; Greig, JA; Lee, WK; ... Baker, AH; + view all (2010) Lentivirus-mediated Reprogramming of Somatic Cells in the Absence of Transgenic Transcription Factors. MOL THER , 18 (12) 2139 - 2145. 10.1038/mt.2010.231.

Knight, SB; Bokhoven, M; Gubta, A; Zhang, F; Antoniou, M; Thrasher, A; ... Takeuchi, Y; + view all (2010) Insertional Mutagenesis by Lentiviral Vectors. In: HUMAN GENE THERAPY. (pp. 496 - 497). MARY ANN LIEBERT INC


Langford-Smith, AWW; Wilkinson, FL; Langford-Smith, KJ; Bennett, W; Howe, S; Thrasher, A; ... Bigger, BW; + view all (2010) Lentiviral Vector-Mediated Stem Cell Gene Therapy for Mucopolysaccharidosis Type IIIA (MPSIIIA). In: HUMAN GENE THERAPY. (pp. 502 - 503).

Ljungman, P; Bregni, M; Brune, M; Cornelissen, J; de Witte, T; Dini, G; ... European Grp Blood Marrow Transpl,; + view all (2010) Allogeneic and autologous transplantation for haematological diseases, solid tumours and immune disorders: current practice in Europe 2009. BONE MARROW TRANSPL , 45 (2) 219 - 234. 10.1038/bmt.2009.141.

Loew, R; Meyer, Y; Kuehlcke, K; Gama-Norton, L; Wirth, D; Hauser, H; ... Schambach, A; + view all (2010) A new PG13-based packaging cell line for stable production of clinical-grade self-inactivating gamma-retroviral vectors using targeted integration. GENE THERAPY , 17 (2) 272 - 280. 10.1038/gt.2009.134.


Macpherson, L; Monypenny, J; Blundell, MP; Cory, GA; Garcia, JT; Thrasher, A; ... Calle, Y; + view all (2010) Tyrosine Phosphorylation of WASP Promotes Calpain Mediated Podosome Disassembly In Myeloid Cells. In: BLOOD. (pp. 638 - 638). AMER SOC HEMATOLOGY

Macpherson, L; Monypenny, J; Blundell, MP; Cory, GO; Tome-Garcia, J; Thrasher, A; ... Calle, Y; + view all (2010) Tyrosine Phosphorylation of WASP Promotes Calpain-Mediated Podosome Disassembly In Myeloid Cells. In: BLOOD. (pp. 638 - 638). AMER SOC HEMATOLOGY

Moncrieffe, H; Nistala, K; Kamhieh, Y; Evans, J; Eddaoudi, A; Eaton, S; Wedderburn, LR; (2010) High Expression of the Ectonucleotidase CD39 on T Cells from the Inflamed Site Identifies Two Distinct Populations, One Regulatory and One Memory T Cell Population. J IMMUNOL , 185 (1) 134 - 143. 10.4049/jimmunol.0803474.

Montiel-Equihua, CA; Antoniou, M; Thrasher, AJ; Gaspar, HB; (2010) Systemic Gene Therapy of SCID-ADA: Improving Transgene Expression in the Erythrocyte Lineage. In: HUMAN GENE THERAPY. (pp. 497 - 497). MARY ANN LIEBERT INC

Mukherjee, S; Santilli, G; Blundell, MP; Almarza, E; Baker, A; Bueren, J; Thrasher, AJ; (2010) Gene-Corrected Neutrophils from Induced Pluripotent Stem Cells Derived from an X-CGD Disease Model. In: HUMAN GENE THERAPY. (pp. 507 - 507). MARY ANN LIEBERT INC


Nibali, L; O'Dea, M; Bouma, G; Parkar, M; Thrasher, AJ; Burns, S; Donos, N; (2010) Genetic Variants Associated With Neutrophil Function in Aggressive Periodontitis and Healthy Controls. J PERIODONTOL , 81 (4) 527 - 534. 10.1902/jop.2010.090543.


Pallant, C; Howe, S; Qasim, W; Kinnon, C; Thrasher, A; (2010) Developing an In Vitro Model of Common Gamma Chain Deficiency for Correction by Zinc Finger Nucleases. In: HUMAN GENE THERAPY. (pp. 511 - 511). MARY ANN LIEBERT INC

Picard, C; Von Bernuth, H; Ghandil, P; Chrabieh, M; Ku, C-L; Abel, L; ... Bossuyt, X; + view all (2010) Clinical features and outcome of patients with IRAK-4 and MyD88 deficiency. Medicine , 89 (6) 403 - 425. 10.1097/MD.0b013e3181fd8ec3.


Qasim, W; Chan, E; Schaller, T; Thrasher, A; Towers, G; (2010) Lentiviral mediated restriction of HIV by TRIM-Cyclophilin fusion proteins. In: HUMAN GENE THERAPY. (pp. 1372 - 1373). MARY ANN LIEBERT INC

Qasim, W; Semenova, E; Thrasher, A; Larcher, F; Di, W; (2010) Preclinical modelling of ex-vivo skin gene therapy for Netherton syndrome. In: HUMAN GENE THERAPY. (pp. 1458 - 1458). MARY ANN LIEBERT INC

Qasim, W; Vink, CA; Thrasher, AJ; (2010) Hybrid Lentiviral Vectors. MOL THER , 18 (7) 1263 - 1267. 10.1038/mt.2010.76.


Samarasinghe, S; Mancao, C; Pule, M; Nawroly, N; Karlsson, H; Brewin, J; ... Amrolia, PJ; + view all (2010) Functional characterization of alloreactive T cells identifies CD25 and CD71 as optimal targets for a clinically applicable allodepletion strategy. BLOOD , 115 (2) 396 - 407. 10.1182/blood-2009-08-235895.

Santilli, G; Brendel, C; Almarza, E; Beilin, C; Blundell, M; Haria, S; ... Thrasher, AJ; + view all (2010) Targeted Lentiviral Gene Therapy to Rescue the X-CGD Phenotype. In: HUMAN GENE THERAPY. (pp. 515 - 515). MARY ANN LIEBERT INC

Semenova, E; Larcher, F; Talbot, G; Harper, JI; Thrasher, AJ; Di, WI; Qasim, W; (2010) Lentiviral Mediated LEKTI Expression Reverses the Netherton Syndrome Phenotype. In: HUMAN GENE THERAPY. (pp. 512 - 512). MARY ANN LIEBERT INC

Semenova, E; Qasim, W; Larcher, F; Talbot, G; Thrasher, AJ; Harper, JI; Di, WL; (2010) Translational development of ex-vivo gene therapy for Netherton syndrome. In: BRITISH JOURNAL OF DERMATOLOGY. (pp. 926 - 926). WILEY-BLACKWELL PUBLISHING, INC

Shaw, SWS; Bollini, S; Nader, KA; Gastadello, A; Mehta, V; Cananzi, M; ... David, AL; + view all (2010) Wide spread and systemic engraftment after in utero autologous transplantation of amniotic fluid mesenchymal stem cells into sheep fetuses. Presented at: UNSPECIFIED.

Shaw, SWS; Bollini, S; Nader, KA; Gastadello, A; Mehta, V; Filppi, E; ... David, AL; + view all (2010) Widespread Engraftment after In Utero Autologous Transplantation of Amniotic Fluid Derived Mesenchymal Stem Cells into Sheep Fetuses. Presented at: 57th Annual Meeting of the Society-for-Gynecologic-Investigation, Orlando, FL.

Slatter, M; Rao, K; Amrolia, P; Flood, T; Abinun, M; Cant, A; ... Veys, P; + view all (2010) UK experience of treosulfan-based conditioning regimens in children with primary immunodeficiency. In: BONE MARROW TRANSPLANTATION. (pp. S73 - S74). NATURE PUBLISHING GROUP

Stein, S; Ott, MG; Schultze-Strasser, S; Jauch, A; Burwinkel, B; Kinner, A; ... Grez, M; + view all (2010) Genomic instability and myelodysplasia with monosomy 7 consequent to EVI1 activation after gene therapy for chronic granulomatous disease. NAT MED , 16 (2) 198 - U105. 10.1038/nm.2088.


Thrasher, AJ; Burns, SO; (2010) WASP: a key immunological multitasker. NAT REV IMMUNOL , 10 (3) 182 - 192. 10.1038/nri2724.


van Til, NP; Sarwari, R; Visser, TP; de Boer, H; Li, Y; Hauer, J; ... Wagemaker, G; + view all (2010) Lentiviral gene therapy of RAG1 SCID: risks and implications for treatment. In: HUMAN GENE THERAPY. (pp. 1445 - 1445). MARY ANN LIEBERT INC


Waddington, SN; Crossley, R; Sheard, V; Howe, SJ; Buckley, SMK; Coughlan, L; ... McKay, TR; + view all (2010) Gene Delivery of a Mutant TGF beta 3 Reduces Markers of Scar Tissue Formation After Cutaneous Wounding. MOL THER , 18 (12) 2104 - 2111. 10.1038/mt.2010.174.

Walshe, D; Gaspar, HB; Thrasher, AJ; Cale, CM; Gilmour, KC; (2010) STAT5 tyrosine phosphorylation for diagnosis and monitoring of patients with severe combined immunodeficiency. In: CLINICAL AND EXPERIMENTAL IMMUNOLOGY. (pp. 2 - 2). WILEY-BLACKWELL PUBLISHING, INC

Ward, E; Chan, E; Gustafsson, K; Jayasinghe, SN; (2010) Combining bio-electrospraying with gene therapy: a novel biotechnique for the delivery of genetic material via living cells. ANALYST , 135 (5) 1042 - 1049. 10.1039/b923307e.

Ward, N.J.; (2010) Lentiviral vectors for treatment of haemophilia. Doctoral thesis, UCL (University College London). Green open access

Ward, NJ; Buckley, SM; Waddington, SN; Nathwani, AC; Tuddenham, EG; Kinnon, C; ... McVey, JH; + view all (2010) Correction of Murine Hemophilia A Using SIN Lentiviral Vectors Expressing Enhanced Human Factor VIII cDNAs. In: HUMAN GENE THERAPY. (pp. 502 - 502). MARY ANN LIEBERT INC

Westerberg, LS; Meelu, P; Baptista, M; Eston, MA; Adamovich, DA; Cotta-de-Almeida, V; ... Snapper, SB; + view all (2010) Activating WASP mutations associated with X-linked neutropenia result in enhanced actin polymerization, altered cytoskeletal responses, and genomic instability in lymphocytes. J EXP MED , 207 (6) 1145 - 1152. 10.1084/jem.20091245.

Williams, DA; Thrasher, AJ; Baum, C; (2010) Transatlantic consortium spotlights need for changes in gene therapy trials. Molecular Therapy , 18 (11) 1892 - 1892. 10.1038/mt.2010.227.

Worth, A.J.J.; (2010) Analysis of the domain specific function of the Wiskott Aldrich Syndrome Protein, in vitro and in vivo. Doctoral thesis, UCL (University College London). Green open access


Xue, SA; Ghorashian, S; Pospori, C; Ahmadi, M; Holler, A; Thomas, S; Stauss, HJ; (2010) Development of CMV-specific T cells for the management of transplantation patients. In: HUMAN GENE THERAPY. (pp. 1422 - 1423). MARY ANN LIEBERT INC


Yeung, J; Esposito, MT; Gandillet, A; Zeisig, BB; Griessinger, E; Bonnet, D; So, CWE; (2010) β-Catenin Mediates the Establishment and Drug Resistance of MLL Leukemic Stem Cells. Cancer Cell , 18 (6) 606 - 618. 10.1016/j.ccr.2010.10.032.


Zhan, H; Thrasher, A; Farzaneh, F; Bhalla, J; Chan, L; Veys, P; ... Qasim, W; + view all (2010) Preparation for a Phase I/II Clinical Trial of T Cell Suicide Gene Therapy Following Haematopoietic Stem Cell Transplantation in Children. In: HUMAN GENE THERAPY. (pp. 509 - 509). MARY ANN LIEBERT INC

Zhang, F; Antoniou, MN; Thrasher, A; (2010) A2UCOE Lentiviral Vector Resists DNA Methylation-Mediated Silencing, Conferring Long-Term Expression in HSCs Following Serial Transplantation In Vivo. In: HUMAN GENE THERAPY. (pp. 514 - 515). MARY ANN LIEBERT INC

Zhang, F; Frost, AR; Blundell, MP; Bales, O; Antoniou, MN; Thrasher, AJ; (2010) A Ubiquitous Chromatin Opening Element (UCOE) Confers Resistance to DNA Methylation-mediated Silencing of Lentiviral Vectors. MOL THER , 18 (9) 1640 - 1649. 10.1038/mt.2010.132.

This list was generated on Sun Jul 27 07:43:26 2014 BST.