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Number of items: 102.

A

Abeyewickreme, A; Thrasher, AJ; Kinnon, C; (2011) Bone morphogenetic protein-4 (BMP4) up regulates key haematopoietic genes in differentiating embryonic stem cells treated with BMP4 short hairpin RNA. Br J Haematol , 155 (5) 638 - 641. 10.1111/j.1365-2141.2011.08759.x.

Acosta-Saltos, C; Gonitel, R; Chavda, S; Acosta-Saltos, A; Rahim, A; Thrasher, A; ... Raivich, G; + view all (2011) Viral expression of GM-CSF: neuroinflammatory response and effects on regeneration. HUM GENE THER , 22 (10) A95 - A95.

Aitchison, KL; Rahim, AA; Hughes, DA; Kinnon, C; Waddington, SN; Howe, SJ; (2011) Lentiviral vectors for gene therapy of Type I Gaucher Disease. HUM GENE THER , 22 (10) A44 - A44.

Ali-Boucetta, H; Al-Jamal, KT; Müller, KH; Li, S; Porter, AE; Eddaoudi, A; ... Kostarelos, K; + view all (2011) Cellular uptake and cytotoxic impact of chemically functionalized and polymer-coated carbon nanotubes. Small , 7 (22) 3230 - 3238. 10.1002/smll.201101004.

Almarza, E; Zhang, F; Santilli, G; Blundell, MP; Howe, SJ; Thornhill, SI; ... Thrasher, AJ; + view all (2011) Correction of SCID-X1 Using an Enhancerless Vav Promoter. HUM GENE THER , 22 (3) 263 - 270. 10.1089/hum.2010.119.

Alonso-Ferrero, ME; Burke, D; Heales, S; Thrasher, A; Gaspar, HB; (2011) Gene therapy for lysosomal storage diseases using an enhanced lentiviral vector delivery system. HUM GENE THER , 22 (10) A44 - A45.

Alvares, CL; Schenk, T; Hulkki, S; Min, T; Vijayaraghavan, G; Yeung, J; ... Morgan, G; + view all (2011) Tyrosine kinase inhibitor insensitivity of non-cycling CD34+ human acute myeloid leukaemia cells with FMS-like tyrosine kinase 3 mutations. BRIT J HAEMATOL , 154 (4) 457 - 465. 10.1111/j.1365-2141.2011.08748.x.

Argyros, O; Wong, SP; Fedonidis, C; Tolmachov, O; Waddington, SN; Howe, SJ; ... Harbottle, RP; + view all (2011) Development of S/MAR minicircles for enhanced and persistent transgene expression in the mouse liver. J Mol Med (Berl) , 89 (5) 515 - 529. 10.1007/s00109-010-0713-3.

B

Bacchelli, C; Buckland, KF; Buckridge, S; Salzer, U; Schneider, P; Thrasher, AJ; Gaspar, HB; (2011) The C76R transmembrane activator and calcium modulator cyclophilin ligand interactor mutation disrupts antibody production and B-cell homeostasis in heterozygous and homozygous mice. J ALLERGY CLIN IMMUN , 127 (5) 1253 - U259. 10.1016/j.jaci.2011.02.037.

Bainbridge, J; Sundaram, V; Robbie, S; Smith, A; Stockman, A; Rubin, G; ... Ali, R; + view all (2011) Gene therapy for eye disease. In: JOURNAL OF MEDICAL GENETICS. (pp. S45 - S45). B M J PUBLISHING GROUP

Bartholomae, CC; Arens, A; Balaggan, KS; Yanez-Munoz, RJ; Montini, E; Howe, SJ; ... Schmidt, M; + view all (2011) Lentiviral Vector Integration Profiles Differ in Rodent Postmitotic Tissues. MOL THER , 19 (4) 703 - 710. 10.1038/mt.2011.19.

Beilin, C; Choudhuri, K; Bouma, G; Thrasher, AJ; Dustin, ML; Burns, SO; (2011) Dendritic cell common G-chain cytokine receptor is required for optimal IL-15 transpresentation to CD4+T cells at the immunological synapse. In: IMMUNOLOGY. (pp. 110 - 110).

Beilin, C.; (2011) Common cytokine receptor γ chain deficiency in dendritic cells: implications for immunity. Doctoral thesis, UCL (University College London).

Binny, C; McIntosh, J; Peruta, M; Kymalainen, H; Tuddenham, E; Waddington, S; ... Nathwani, A; + view all (2011) AAV-mediated gene transfer in the perinatal period results in expression of FVII at levels that protect against fatal spontaneous haemorrhage. HUMAN GENE THERAPY , 22 (10) A45 - A45.

Binny, C; McIntosh, J; Peruta, M; Kymalainen, H; Tuddenham, E; Waddington, S; ... Nathwani, A; + view all (2011) AAV-mediated gene transfer in the perinatal period results in expression of FVII at levels that protect against fatal spontaneous haemorrhage. HUMAN GENE THERAPY , 22 (10) A45 - A45.

Booth, C; Gaspar, HB; Thrasher, AJ; (2011) Gene therapy for primary immunodeficiency. Curr Opin Pediatr , 23 (6) 659 - 666. 10.1097/MOP.0b013e32834cd67a.

Booth, C; Gilmour, KC; Veys, P; Gennery, AR; Slatter, MA; Chapel, H; ... Gaspar, HB; + view all (2011) X-linked lymphoproliferative disease due to SAP/SH2D1A deficiency: a multicenter study on the manifestations, management and outcome of the disease. Blood , 117 (1) 53 - 62. 10.1182/blood-2010-06-284935.

Bouma, G; Mendoza-Naranjo, A; Blundell, MP; de Falco, E; Parsley, KL; Burns, SO; Thrasher, AJ; (2011) Cytoskeletal remodeling mediated by WASp in dendritic cells is necessary for normal immune synapse formation and T-cell priming. BLOOD , 118 (9) 2492 - 2501. 10.1182/blood-2011-03-340265.

Bouma, G; Thrasher, AJ; (2011) Disorders of phagocyte function. In: UNSPECIFIED (263 - 272).

Brown, L; Xu-Bayford, J; Allwood, Z; Slatter, M; Cant, A; Davies, EG; ... Gaspar, HB; + view all (2011) Neonatal diagnosis of severe combined immunodeficiency leads to significantly improved survival outcome: the case for newborn screening. BLOOD , 117 (11) 3243 - 3246. 10.1182/blood-2010-08-300384.

Brown, L; Xu-Bayford, J; Allwood, Z; Slatter, M; Cant, A; Davies, EG; ... Gaspar, HB; + view all (2011) Neonatal Diagnosis of Severe Combined Immunodeficiency Leads to Significantly Improved Survival Outcome: The Case for Newborn Screening EDITORIAL COMMENT. OBSTET GYNECOL SURV , 66 (7) 398 - 399. 10.1097/OGX.0b013e3182338432.

Buckland, KF; Ramaprakash, H; Murray, LA; Carpenter, KJ; Choi, ES; Kunkel, SL; ... Hogaboam, CM; + view all (2011) Triggering Receptor Expressed on Myeloid cells-1 (TREM-1) Modulates Immune Responses to Aspergillus fumigatus During Fungal Asthma in Mice. IMMUNOL INVEST , 40 (7-8) 692 - 722. 10.3109/08820139.2011.578270.

C

Carmo, M; Montiel-Equihua, CA; Schambach, A; Baum, C; Thrasher, AJ; Gaspar, HB; (2011) Development of gene therapy for haemophagocytic lymphohistiocytosis (HLH) due to perforin deficiency. HUM GENE THER , 22 (10) A46 - A47.

Chan, E; Schaller, T; Thrasher, A; Towers, G; Qasim, W; (2011) Lentivirus mediated protection against HIV-1 using a human TRIM21-Cyclophilin A fusion protein. HUM GENE THER , 22 (10) A68 - A68.

Cooray, S; Gilmour, KC; Parsley, KL; Adams, S; Howe, SJ; Al Ghonaium, A; ... Thrasher, AJ; + view all (2011) Persistence of a polyclonal T-cell repertoire in patients with SCID-X1 following gene therapy. HUM GENE THER , 22 (10) A42 - A42.

Cooray, S; Gilmour, KC; Parsley, KL; Zhang, F; Bjorkegren, E; Bayford, J; ... Gaspar, HB; + view all (2011) Hematopoietic stem cell gene therapy for adenosine deaminase-deficient severe combined immunodeficiency leads to long-term immunological recovery and metabolic correction. HUM GENE THER , 22 (10) A40 - A40.

D

de Boer, J; Yeung, J; Ellu, J; Ramanujachar, R; Bornhauser, B; Solarska, O; ... Brady, HJM; + view all (2011) The E2A-HLF oncogenic fusion protein acts through Lmo2 and Bcl-2 to immortalize hematopoietic progenitors. LEUKEMIA , 25 (2) 321 - 330. 10.1038/leu.2010.253.

Deichmann, A; Brugman, MH; Bartholomae, CC; Schwarzwaelder, K; Verstegen, MMA; Howe, SJ; ... Wagemaker, G; + view all (2011) Insertion Sites in Engrafted Cells Cluster Within a Limited Repertoire of Genomic Areas After Gammaretroviral Vector Gene Therapy. MOL THER , 19 (11) 2031 - 2039. 10.1038/mt.2011.178.

Di, WL; Larcher, F; Semenova, E; Talbot, GE; Harper, JI; Del Rio, M; ... Qasim, W; + view all (2011) Ex-vivo Gene Therapy Restores LEKTI Activity and Corrects the Architecture of Netherton Syndrome-derived Skin Grafts. MOL THER , 19 (2) 408 - 416. 10.1038/mt.2010.201.

Dong, R; Himoudi, N; Basu, BP; Anderson, J; Moulding, D; Bouma, G; ... Duncan, A; + view all (2011) Cells with dendritic cell morphology and immunophenotype, binuclear morphology, and immunosuppressive function in dendritic cell cultures. Cellular Immunology , 272 (1) 1 - 10. 10.1016/j.cellimm.2011.09.012.

Dong, R; Moulding, D; Himoudi, N; Adams, S; Bouma, G; Eddaoudi, A; ... Anderson, J; + view all (2011) Cells with dendritic cell morphology and immunophenotype, binuclear morphology, and immunosuppressive function in dendritic cell cultures. Cell Immunol , 272 (1) 1 - 10. 10.1016/j.cellimm.2011.09.012.

F

Farmer, S; Lorain, S; Thrasher, A; Garcia, L; Muntoni, F; Conti, F; (2011) Correction of FKRP function via RNA trans-splicing. In: NEUROMUSCULAR DISORDERS. (pp. S8 - S8). PERGAMON-ELSEVIER SCIENCE LTD

Farmer, S; Lorain, S; Thrasher, A; Garcia, L; Muntoni, F; Conti, F; (2011) Correction of FKRP function via RNA trans-splicing. In: NEUROMUSCULAR DISORDERS. (pp. 719 - 720). PERGAMON-ELSEVIER SCIENCE LTD

Fassone, E; Duncan, AJ; Taanman, JW; Pagnamenta, AT; Sadowski, M; Holand, T; ... Rahman, S; + view all (2011) Mutations in the novel chaperone FOXRED1 cause mitochondrial complex I deficiency. In: NEUROMUSCULAR DISORDERS. (pp. S19 - S19). PERGAMON-ELSEVIER SCIENCE LTD

Fassone, E; Duncan, AJ; Taanman, JW; Pagnamenta, AT; Sadowski, MI; Holand, T; ... Rahman, S; + view all (2011) BIOCHEMICAL AND MOLECULAR ANALYSIS IN MITOCHONDRIAL COMPLEX I DEFICIENT CHILDREN. In: JOURNAL OF INHERITED METABOLIC DISEASE. (pp. S162 - S162).

Fassone, E; Duncan, AJ; Taanman, JW; Pagnamenta, AT; Sadowski, MI; Holand, T; ... Rahman, S; + view all (2011) FOXRED1 mutations are a novel cause of mitochondrial complex I deficiency. In: NEUROPATHOLOGY AND APPLIED NEUROBIOLOGY. (pp. 37 - 37). WILEY-BLACKWELL PUBLISHING, INC

Felgentreff, K; Perez-Becker, R; Speckmann, C; Schwarz, K; Kalwak, K; Markelj, G; ... Ehl, S; + view all (2011) Clinical and immunological manifestations of patients with atypical severe combined immunodeficiency. CLIN IMMUNOL , 141 (1) 73 - 82. 10.1016/j.clim.2011.05.007.

G

Galy, A; Thrasher, AJ; (2011) Gene therapy for the Wiskott-Aldrich syndrome. CURR OPIN ALLERGY CL , 11 (6) 545 - 550. 10.1097/ACI.0b013e32834c230c.

Gaspar, HB; (2011) Induced pluripotent stem cells and primary immunodeficiencies: A new frontier reached, a new world beyond? J ALLERGY CLIN IMMUN , 127 (6) 1408 - 1409. 10.1016/j.jaci.2011.02.038.

Gaspar, HB; Cooray, S; Gilmour, KC; Parsley, KL; Adams, S; Howe, SJ; ... Thrasher, AJ; + view all (2011) Long-Term Persistence of a Polyclonal T Cell Repertoire After Gene Therapy for X-Linked Severe Combined Immunodeficiency. SCI TRANSL MED , 3 (97) , Article 97ra79. 10.1126/scitranslmed.3002715.

Gaspar, HB; Cooray, S; Gilmour, KC; Parsley, KL; Howe, SJ; Bayford, J; ... Al Ghonaium, A; + view all (2011) Immunodeficiency: Long-term persistence of a polyclonal t cell repertoire after gene therapy for X-linked severe combined immunodeficiency. Science Translational Medicine , 3 (97) 10.1126/scitranslmed.3002715.

Gaspar, HB; Cooray, S; Gilmour, KC; Parsley, KL; Zhang, F; Adams, S; ... Thrasher, AJ; + view all (2011) Hematopoietic Stem Cell Gene Therapy for Adenosine Deaminase-Deficient Severe Combined Immunodeficiency Leads to Long-Term Immunological Recovery and Metabolic Correction. SCI TRANSL MED , 3 (97) , Article 97ra80. 10.1126/scitranslmed.3002716.

Gaspar, HB; Cooray, S; Gilmour, KC; Parsley, KL; Zhang, F; Bjorkegren, E; ... Petropolou, T; + view all (2011) Immunodeficiency: Hematopoietic stem cell gene therapy for adenosine deaminase-deficient severe combined immunodeficiency leads to long-term immunological recovery and metabolic correction. Science Translational Medicine , 3 (97) 10.1126/scitranslmed.3002716.

Gholam, C; Grigoriadou, S; Gilmour, KC; Gaspar, HB; (2011) Familial haemophagocytic lymphohistiocytosis: advances in the genetic basis, diagnosis and management. CLIN EXP IMMUNOL , 163 (3) 271 - 283. 10.1111/j.1365-2249.2010.04302.x.

Grez, M; Reichenbach, J; Schwable, J; Seger, R; Dinauer, MC; Thrasher, AJ; (2011) Gene Therapy of Chronic Granulomatous Disease: The Engraftment Dilemma. MOL THER , 19 (1) 28 - 35. 10.1038/mt.2010.232.

H

Hacein-Bey-Abina, S; Caccaveli, L; Touzot, F; Dal-Cortivo, L; Heritier, S; Frange, P; ... Cavazzana-Calvo, M; + view all (2011) Efficacy of gene therapy for X-linked severe combined immunodeficiency: update on trial No.1 follow-up and preliminary results of multicentric collaborative trial No. 2 (Paris - Boston - London). HUMAN GENE THERAPY , 22 (10) A40 - A40.

Hiwarkar, P; Rao, A; (2011) Revisiting Darwinism explains extinction of fetal erythroid progenitors in a leukaemogenic model of a paediatric myeloproliferative neoplasm. Br J Haematol , 155 (1) 2 - ?. 10.1111/j.1365-2141.2011.08731.x.

Hiwarkar, P; Shaw, BE; Tredger, JM; Brown, NW; Kulkarni, S; Saso, R; ... Potter, MN; + view all (2011) Mycophenolic acid trough level monitoring: relevance in acute and chronic graft versus host disease and its relation with albumin. CLIN TRANSPLANT , 25 (2) 222 - 227. 10.1111/j.1399-0012.2010.01226.x.

Huston, MW; van Til, NP; Visser, TP; Arshad, S; Brugman, MH; Cattoglio, C; ... Wagemaker, G; + view all (2011) Correction of Murine SCID-X1 by Lentiviral Gene Therapy Using a Codon-optimized IL2RG Gene and Minimal Pretransplant Conditioning. MOL THER , 19 (10) 1867 - 1877. 10.1038/mt.2011.127.

J

Jonuschies, J; Boldrin, L; Thrasher, A; Morgan, JE; Muntoni, F; (2011) Assessment of potential promoters for lentiviral gene therapy in DMD. HUM GENE THER , 22 (10) A5 - A5.

Jonuschies, J; Boldrin, L; Thrasher, A; Morgan, JE; Muntoni, F; (2011) Assessment of potential promoters for lentiviral gene therapy in DMD. HUM GENE THER , 22 (10) A62 - A63.

K

Kallinikou, K; Anjos-Afonso, F; Blundell, MP; Ings, SJ; Kassen, D; Thrasher, AJ; ... Yong, K; + view all (2011) CD26 Inhibition Can Aid the Homing of Cytokine Activated Mobilized Peripheral Blood (MPB)CD34+Cells to the Bone Marrow (BM) but a Ligand Dependent Attachment Defect Prevents Their Long Term Retention and Subsequent Engraftment. In: BLOOD. (pp. 68 - 68).

Kao, VYC; Waddington, S; Equihua, CM; Thrasher, AJ; Antoniou, MN; (2011) Curative F.IX production from low-dose UCOE-lentiviral vectors. HUM GENE THER , 22 (10) A110 - A110.

Kenny, GD; Kamaly, N; Kalber, TL; Brody, LP; Sahuri, M; Shamsaei, E; ... Bell, JD; + view all (2011) Novel multifunctional nanoparticle mediates siRNA tumour delivery, visualisation and therapeutic tumour reduction in vivo. J CONTROL RELEASE , 149 (2) 111 - 116. 10.1016/j.jconrel.2010.09.020.

Kudsiova, L; Ho, J; Fridrich, B; Harvey, R; Keppler, M; Ng, T; ... Lawrence, MJ; + view all (2011) Lipid chain geometry of C14 glycerol-based lipids: effect on lipoplex structure and transfection. MOL BIOSYST , 7 (2) 422 - 436. 10.1039/c0mb00149j.

Kwok, A; Hart, SL; (2011) Comparative structural and functional studies of nanoparticle formulations for DNA and siRNA delivery. NANOMED-NANOTECHNOL , 7 (2) 210 - 219. 10.1016/j.nano.2010.07.005.

L

Langford-Smith, A; Wilkinson, F; Langford-Smith, KJ; Sergijenko, A; Bennett, W; Howe, S; ... Bigger, B; + view all (2011) Lentiviral vector enhanced haematopoietic stem cell gene therapy for mucopolysaccharidosis type IIIA. In: BONE MARROW TRANSPLANTATION. (pp. S316 - S316).

M

Malik, SJ; Kenny, GD; Hajnal, JV; (2011) Slice profile correction for transmit sensitivity mapping using actual flip angle imaging. Magn Reson Med , 65 (5) 1393 - 1399. 10.1002/mrm.22739.

Mandegar, MA; Moralli, D; Khoja, S; Cowley, S; Chan, DYL; Yusuf, M; ... Monaco, ZL; + view all (2011) Functional human artificial chromosomes are generated and stably maintained in human embryonic stem cells. HUM MOL GENET , 20 (15) 2905 - 2913. 10.1093/hmg/ddr144.

Manunta, MDI; McAnulty, RJ; Tagalakis, AD; Bottoms, SE; Campbell, F; Hailes, HC; ... Hart, SL; + view all (2011) Nebulisation of Receptor-Targeted Nanocomplexes for Gene Delivery to the Airway Epithelium. PLoS ONE , 6 (10) , Article e26768. 10.1371/journal.pone.0026768. Green and gold open access
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Manunta, MDI; McAnulty, RJ; Tagalakis, AD; Bottoms, SE; Campbell, F; Hailes, HC; ... Hart, SL; + view all (2011) Nebulisation of Receptor-Targeted Nanocomplexes for Gene Delivery to the Airway Epithelium. PLoS ONE , 6 (10) , Article e26768. 10.1371/journal.pone.0026768. Green and gold open access
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Manunta, MDI; McAnulty, RJ; Tagalakis, AD; Bottoms, SE; Campbell, F; Hailes, HC; ... Hart, SL; + view all (2011) Nebulisation of Receptor-Targeted Nanocomplexes for Gene Delivery to the Airway Epithelium. PLOS ONE , 6 (10) , Article e26768. 10.1371/journal.pone.0026768. Green and gold open access
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McKay, TR; Rahim, AA; Buckley, SM; Ward, NJ; Chan, JK; Howe, SJ; Waddington, SN; (2011) Perinatal gene transfer to the liver. Curr Pharm Des , 17 (24) 2528 - 2541.

Mendoza-Naranjo, A; Bouma, G; Pereda, C; Ramirez, M; Webb, KF; Tittarelli, A; ... Salazar-Onfray, F; + view all (2011) Functional Gap Junctions Accumulate at the Immunological Synapse and Contribute to T Cell Activation. J IMMUNOL , 187 (6) 3121 - 3132. 10.4049/jimmunol.1100378.

Metelo, J; Ward, N; Thrasher, AJ; Burns, SO; (2011) Lentivectors Are Efficient Tools to Manipulate the Dendritic Cell Cytoskeleton. CYTOSKELETON , 68 (8) 434 - 445. 10.1002/cm.20521.

Montiel-Equihua, CA; Zhang, L; Knight, S; Collins, M; Saadeh, H; Schulz, R; ... Gaspar, HB; + view all (2011) Development of a gene expression system for enhanced erythroid expression. HUMAN GENE THERAPY , 22 (10) A105 - A105.

Monypenny, J; Chou, HC; Banon-Rodriguez, I; Thrasher, AJ; Anton, IM; Jones, GE; Calle, Y; (2011) Role of WASP in cell polarity and podosome dynamics of myeloid cells. EUR J CELL BIOL , 90 (2-3) 198 - 204. 10.1016/j.ejcb.2010.05.009.

Moratto, D; Giliani, S; Bonfim, C; Mazzolari, E; Fischer, A; Ochs, HD; ... Notarangelo, LD; + view all (2011) Long-term outcome and lineage-specific chimerism in 194 patients with Wiskott-Aldrich syndrome treated by hematopoietic cell transplantation in the period 1980-2009: an international collaborative study. BLOOD , 118 (6) 1675 - 1684. 10.1182/blood-2010-11-319376.

Mukherjee, S; Santilli, G; Blundell, MP; Navarro, S; Bueren, JA; Thrasher, AJ; (2011) Generation of Functional Neutrophils from a Mouse Model of X-Linked Chronic Granulomatous Disorder Using Induced Pluripotent Stem Cells. PLOS ONE , 6 (3) , Article e17565. 10.1371/journal.pone.0017565. Green and gold open access
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Mukherjee, S; Thrasher, AJ; (2011) iPSCs: Unstable Origins? MOL THER , 19 (7) 1188 - 1190. 10.1038/mt.2011.116.

MUKHERJEE, S; Thrasher, AJ; (2011) iPSCs:Unstable Origins? Molecular Therapy , 19 (7) 1188 - 1190. 10.1038/mt.2011.116.

Mukherjee, S; Thrasher, AJ; (2011) Progress and Prospects: Advancements in Retroviral Vector Design, Generation, and Application. HUM GENE THER , 22 (10) 1171 - 1174. 10.1089/hum.2011.2523.

P

Palendira, U; Low, C; Chan, A; Hislop, AD; Ho, E; Phan, TG; ... Tangye, SG; + view all (2011) Molecular Pathogenesis of EBV Susceptibility in XLP as Revealed by Analysis of Female Carriers with Heterozygous Expression of SAP. PLOS BIOLOGY , 9 (11) , Article e1001187. 10.1371/journal.pbio.1001187. Green and gold open access
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Pallant, C; Cathomen, T; Dannemann, N; Quasim, W; Naldini, L; Kinnon, C; ... Thrasher, A; + view all (2011) Targeting models of severe combined immunodeficiency for correction by zinc finger nucleases. HUM GENE THER , 22 (10) A41 - A41.

Pike-Overzet, K; Rodijk, M; Ng, YY; Baert, MRM; Lagresle-Peyrou, C; Schambach, A; ... Staal, FJT; + view all (2011) Correction of murine Rag1 deficiency by self-inactivating lentiviral vector-mediated gene transfer. LEUKEMIA , 25 (9) 1471 - 1483. 10.1038/leu.2011.106.

Pizzolla, A; Gelderman, KA; Hultqvist, M; Vestberg, M; Gustafsson, K; Mattsson, R; Holmdahl, R; (2011) CD68-expressing cells can prime T cells and initiate autoimmune arthritis in the absence of reactive oxygen species. Eur J Immunol , 41 (2) 403 - 412. 10.1002/eji.201040598.

Q

Qasim, W; Derniame, S; Gilmour, K; Chiesa, R; Weber, M; Adams, S; ... Gaspar, H; + view all (2011) Third-party virus-specific T cells eradicate adenoviraemia but trigger bystander graft-versus-host disease. BRIT J HAEMATOL , 154 (1) 150 - 153. 10.1111/j.1365-2141.2011.08579.x.

R

Rocca, C; Abdul-Razak, HH; Estevez, FJM; Guenechea, G; Howe, SJ; Holmes, MC; ... Yanez-Munoz, RJ; + view all (2011) ZFN-driven gene targeting to correct mouse Prkdc scid deficiency. HUM GENE THER , 22 (10) A44 - A44.

S

Samarasinghe, S; Steward, C; Hiwarkar, P; Bonney, D; Keogh, S; Rao, K; ... Veys, P; + view all (2011) ALEMTUZUMAB-BASED CONDITIONING PROTOCOLS FOR PAEDIATRIC MATCHED UNRELATED DONOR TRANSPLANTS FOR SEVERE APLASTIC ANAEMIA: AN IMPORTANT ALTERNATIVE TO TBI CONTAINING REGIMENS. In: BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION. (pp. S186 - S187). ELSEVIER SCIENCE INC

Santilli, G; Almarza, E; Brendel, C; Choi, U; Beilin, C; Blundell, MP; ... Thrasher, AJ; + view all (2011) Biochemical Correction of X-CGD by a Novel Chimeric Promoter Regulating High Levels of Transgene Expression in Myeloid Cells. MOL THER , 19 (1) 122 - 132. 10.1038/mt.2010.226.

Santilli, G; Kehl, E; Parsley, K; Cooray, S; Buckland, K; Blundell, M; ... Thrasher, AJ; + view all (2011) Development of a clinical trial of gene therapy for X-CGD using the pCCLCHIMGp91WPRE4 lentiviral vector. HUM GENE THER , 22 (10) A52 - A52.

Semenova, E; Di, WL; Larcher, F; Ghani, S; Harper, J; Thrasher, A; Qasim, W; (2011) Human involucrin promoter resists spreading methylation and supports compartment specific gene expression in engineered skin grafts. HUM GENE THER , 22 (10) A52 - A52.

Shaw, SW; David, AL; Blundell, M; Howe, S; Pipino, C; Maghsoudlou, P; ... De Coppi, P; + view all (2011) Sheep amniotic fluid derived CD34+stem cells engraft in NOD-SCID gamma mice and in lambs after prenatal autologous transplantation. Presented at: UNSPECIFIED.

Shaw, SWS; Bollini, S; Nader, KA; Gastadello, A; Mehta, V; Filppi, E; ... David, AL; + view all (2011) Autologous Transplantation of Amniotic Fluid-Derived Mesenchymal Stem Cells Into Sheep Fetuses. CELL TRANSPLANT , 20 (7) 1015 - 1031. 10.3727/096368910X543402.

Skucek, E; Butler, S; Gaspar, HB; Titman, P; (2011) Social outcome in children treated by haematopoietic cell transplant for congenital immunodeficiency. BONE MARROW TRANSPL , 46 (10) 1314 - 1320. 10.1038/bmt.2010.318.

Slatter, MA; Rao, K; Amrolia, P; Flood, T; Abinun, M; Hambleton, S; ... Veys, P; + view all (2011) Treosulfan-based conditioning regimens for hematopoietic stem cell transplantation in children with primary immunodeficiency: United Kingdom experience. BLOOD , 117 (16) 4367 - 4375. 10.1182/blood-2010-10-312082.

Smith, L-L; Yeung, J; Zeisig, BB; Popov, N; Huijbers, I; Barnes, J; ... So, CWE; + view all (2011) Functional Crosstalk between Bmi1 and MLL/Hoxa9 Axis in Establishment of Normal Hematopoietic and Leukemic Stem Cells. Cell Stem Cell , 8 (6) 649 - 662. 10.1016/j.stem.2011.05.004.

Surman, AJ; Bonnet, CS; Lowe, MP; Kenny, GD; Bell, JD; Tóth, E; Vilar, R; (2011) A pyrophosphate-responsive gadolinium(III) MRI contrast agent. Chemistry , 17 (1) 223 - 230. 10.1002/chem.201001397.

Surman, AJ; Kenny, GD; Kumar, DK; Bell, JD; Casey, DR; Vilar, R; (2011) Targeting of anionic membrane species by lanthanide(III) complexes: towards improved MRI contrast agents for apoptosis. Chem Commun (Camb) , 47 (37) 10245 - 10247. 10.1039/c1cc13284a.

T

Tagalakis, AD; Grosse, SM; Meng, QH; Mustapa, MFM; Kwok, A; Salehi, SE; ... Hart, SL; + view all (2011) Integrin-targeted nanocomplexes for tumour specific delivery and therapy by systemic administration. BIOMATERIALS , 32 (5) 1370 - 1376. 10.1016/j.biomaterials.2010.10.037.

Tagalakis, AD; He, L; Saraiva, L; Gustafsson, KT; Hart, SL; (2011) Receptor-targeted liposome-peptide nanocomplexes for siRNA delivery. BIOMATERIALS , 32 (26) 6302 - 6315. 10.1016/j.biomaterials.2011.05.022.

Thrasher, A; (2011) Gene therapy for immunodeficiency. HUMAN GENE THERAPY , 22 (10) A5 - A6.

Thrasher, AJ; Segal, AW; (2011) A phagocyte dilemma... NAT IMMUNOL , 12 (3) 201 - 202. 10.1038/ni0311-201.

Tolar, J; Adair, JE; Antoniou, M; Bartholomae, CC; Becker, PS; Blazar, BR; ... Thrasher, AJ; + view all (2011) Stem Cell Gene Therapy for Fanconi Anemia: Report from the 1st International Fanconi Anemia Gene Therapy Working Group Meeting. MOL THER , 19 (7) 1193 - 1198. 10.1038/mt.2011.78.

W

Ward, NJ; Buckley, SMK; Rahim, AA; McVey, JH; Thrasher, AJ; Waddington, SN; (2011) Optimised vectors for the treatment of haemophilia A. HUM GENE THER , 22 (10) A109 - A109.

Ward, NJ; Buckley, SMK; Waddington, SN; VandenDriessche, T; Chuah, MKL; Nathwani, AC; ... McVey, JH; + view all (2011) Codon optimization of human factor VIII cDNAs leads to high-level expression. BLOOD , 117 (3) 798 - 807. 10.1182/blood-2010-05-282707.

Williams, DA; Thrasher, AJ; (2011) Out of harm's way. Nature Biotechnology , 29 (1) 41 - 42. 10.1038/nbt.1750.

Worth, A; Conyers, R; Cohen, J; Jagani, M; Chiesa, R; Rao, K; ... Amrolia, PJ; + view all (2011) Pre-emptive rituximab based on viraemia and T cell reconstitution: a highly effective strategy for the prevention of Epstein-Barr virus-associated lymphoproliferative disease following stem cell transplantation. BRIT J HAEMATOL , 155 (3) 377 - 385. 10.1111/j.1365-2141.2011.08855.x.

Y

Yan, MY; Himoudi, N; Basu, BP; Wallace, R; Poon, E; Adams, S; ... Anderson, J; + view all (2011) Increased PRAME antigen-specific killing of malignant cell lines by low avidity CTL clones, following treatment with 5-Aza-2'-Deoxycytidine. CANCER IMMUNOL IMMUN , 60 (9) 1243 - 1255. 10.1007/s00262-011-1024-4.

Z

Zhan, H; Farzaneh, F; Gilmour, K; Bhalla, J; Chan, L; Fehse, B; ... Qasim, W; + view all (2011) Pathway to delivery of a gene modified T cell Investigational Medicinal Product (IMP). HUM GENE THER , 22 (10) A74 - A75.

Zhang, F; Thrasher, A; Antoniou, M; (2011) The lentiviral vector containing UCOE element driving IL2 receptor gene confers a long term immuno-reconstitution in mouse model of SCID-X1. HUM GENE THER , 22 (10) A110 - A110.

Zhang, L; Montiel-Equihua, CA; Thrasher, AJ; Gaspar, HB; (2011) Dr Lin Zhang. HUMAN GENE THERAPY , 22 (10) A53 - A54.

This list was generated on Sun Apr 20 04:12:01 2014 BST.